RG7800 hydrochloride

MedChem Express

RG7800 hydrochloride

10

99.59%

C24H28N6O.xHCl

RG7800 hydrochloride is an orally active SMN2 splicing modulator, with EC1.5xs of 23 nM and 87 nM for SMN2 splicing and SMN protein; RG7800 hydrochloride has the potential to treat spinal muscular atrophy.

CC1=CC(C2CCN(C)CC2)=CN3C1=NC(C4=NN(C=C(C)N=C5CC)C5=C4)=CC3=O.[xHCl]

2°C to 8°C,-20°C,-80°C

12352200